Our project to reconstitute progranulin expression using engineered hematopoietic stem cells was selected for the Alliance for Innovative Medicines program

September, 2020

A joint venture with Takeda to accelerate the development of this cell-based therapy

The Orphan Disease Center renews funding for our research on MPSI

September, 2020

Optimizing cell selection and conditioning regimens for autologous transplantation of human genome-edited hematopoietic stem cells to treat MPSI

Gomez-Ospina Lab awarded a grant from Friedreich's Ataxia research alliance

September, 2020

Role of hematopoeitic stem cell transplantation in FRDA

Gomez-Ospina Lab awarded MCHRI TIPS to work on Progranulin deficiency

June, 2020

A trans-disciplinary project with Dr. Monther Abu-Remaileh

Award for Research by a Young Investigator (Abbott Nutrition) for Dr. Gomez-Ospina. Western Society for Pediatric Research (WSPR)

February, 2020

William K. Bowes Jr. Award in Medical Genetics

2019

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https://personalizedmedicine.partners.org/Education/Bowes-Award/Default.aspx

Young Investigator Award

2018

14th annual WORLDSymposium on lysosomal storage diseases